Repeated AAV9 Titer Determination in a Presymptomatic SMA Patient with Three SMN2 Gene Copies - A Case Report

Astrid Eisenkölbl, Manuel Pühringer

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)493-498
Number of pages6
JournalJournal of Neuromuscular Diseases
Volume11
Issue number2
DOIs
Publication statusPublished - 05 Mar 2024

Fields of science

  • 302035 Paediatrics and adolescent medicine

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