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Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial

  • R Savarirayan
  • , DG Hoernschemeyer
  • , M Ljungberg
  • , YA Zarate
  • , CA Bacino
  • , MB Bober
  • , JM Legare
  • , Wolfgang Högler
  • , T Quattrin
  • , MJ Abuzzahab
  • , PL Hofman
  • , KK White
  • , NS Ma
  • , Dirk Schnabel
  • , SB Sousa
  • , M Mao
  • , Alden Smith
  • , M Chakraborty
  • , A Giwa
  • , Bent Winding
  • C McDonnell

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article number102258
Number of pages10
JournalEClinicalMedicine
Volume65
DOIs
Publication statusPublished - Nov 2023

Fields of science

  • 302035 Paediatrics and adolescent medicine

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