Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial

R Savarirayan; DG Hoernschemeyer; M Ljungberg; YA Zarate; CA Bacino; MB Bober; JM Legare; Wolfgang Högler; T Quattrin; MJ Abuzzahab; PL Hofman; KK White; NS Ma; Dirk Schnabel; SB Sousa; M Mao; Alden Smith; M Chakraborty; A Giwa; Bent Winding; C McDonnell

doi:10.1016/j.eclinm.2023.102258

Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial

R Savarirayan, DG Hoernschemeyer, M Ljungberg, YA Zarate, CA Bacino, MB Bober, JM Legare, Wolfgang Högler, T Quattrin, MJ Abuzzahab, PL Hofman, KK White, NS Ma, Dirk Schnabel, SB Sousa, M Mao, Alden Smith, M Chakraborty, A Giwa, Bent WindingC McDonnell

Department of Pediatrics and Adolescent Medicine

Research output: Contribution to journal › Article › peer-review

Original language	English
Article number	102258
Number of pages	10
Journal	EClinicalMedicine
Volume	65
DOIs	https://doi.org/10.1016/j.eclinm.2023.102258
Publication status	Published - Oct 2023

Fields of science

302035 Paediatrics and adolescent medicine

Access to Document

10.1016/j.eclinm.2023.102258

Cite this

Savarirayan, R., Hoernschemeyer, DG., Ljungberg, M., Zarate, YA., Bacino, CA., Bober, MB., Legare, JM., Högler, W., Quattrin, T., Abuzzahab, MJ., Hofman, PL., White, KK., Ma, NS., Schnabel, D., Sousa, SB., Mao, M., Smith, A., Chakraborty, M., Giwa, A., ... McDonnell, C. (2023). Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial. EClinicalMedicine, 65, Article 102258. https://doi.org/10.1016/j.eclinm.2023.102258

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title = "Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial",

author = "R Savarirayan and DG Hoernschemeyer and M Ljungberg and YA Zarate and CA Bacino and MB Bober and JM Legare and Wolfgang H{\"o}gler and T Quattrin and MJ Abuzzahab and PL Hofman and KK White and NS Ma and Dirk Schnabel and SB Sousa and M Mao and Alden Smith and M Chakraborty and A Giwa and Bent Winding and C McDonnell",

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Savarirayan, R, Hoernschemeyer, DG, Ljungberg, M, Zarate, YA, Bacino, CA, Bober, MB, Legare, JM, Högler, W, Quattrin, T, Abuzzahab, MJ, Hofman, PL, White, KK, Ma, NS, Schnabel, D, Sousa, SB, Mao, M, Smith, A, Chakraborty, M, Giwa, A, Winding, B & McDonnell, C 2023, 'Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial', EClinicalMedicine, vol. 65, 102258. https://doi.org/10.1016/j.eclinm.2023.102258

TY - JOUR

T1 - Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial

AU - Savarirayan, R

AU - Hoernschemeyer, DG

AU - Ljungberg, M

AU - Zarate, YA

AU - Bacino, CA

AU - Bober, MB

AU - Legare, JM

AU - Högler, Wolfgang

AU - Quattrin, T

AU - Abuzzahab, MJ

AU - Hofman, PL

AU - White, KK

AU - Ma, NS

AU - Schnabel, Dirk

AU - Sousa, SB

AU - Mao, M

AU - Smith, Alden

AU - Chakraborty, M

AU - Giwa, A

AU - Winding, Bent

AU - McDonnell, C

PY - 2023/10

Y1 - 2023/10

U2 - 10.1016/j.eclinm.2023.102258

DO - 10.1016/j.eclinm.2023.102258

M3 - Article

SN - 2589-5370

VL - 65

JO - EClinicalMedicine

JF - EClinicalMedicine

M1 - 102258

ER -